Why This Summit Is Unmissable for Biotech Decision-Makers

Advance Your RNA-Targeted Small Molecule Programs With Insights From Industry Peers.

The RNA-targeted small molecule landscape is reaching a crucial inflection point. With increasing clinical validation, growing pharma interest, and significant scientific innovation, biotech leaders must determine where to invest, how to differentiate their platforms, and what it will take to successfully progress programs toward commercialization.

This summit brings together the founders, CSOs, CEOs, platform innovators, and strategic decision-makers shaping the future of RNA-targeted therapeutics.

Biotech Leaders Watching

Challenges We Help Solve

Challenges Solved RNA DDD Number 1

Differentiating Your Platform in a Crowded Market

Understand how successful companies are defining clear competitive advantages and attracting strategic attention.

Challenges Solved RNA DDD Number 2

Advancing From Discovery to Clinical Validation

Learn how leaders are overcoming key scientific and operational hurdles as programs mature.

Challenges Solved RNA DDD Number 3

Securing Strategic Partnerships & Investment

Benchmark approaches for attracting pharma partnerships, investors, and collaborators.

Challenges Solved RNA DDD Number 4

Staying Ahead of the Competitive Landscape

Gain visibility into emerging technologies, companies, and therapeutic opportunities.

Challenges Solved RNA DDD Number 5

Identifying the Next Major Growth Opportunities

Understand which scientific and commercial trends are likely to shape the field over the next five years.

Priority Sessions for Biotech Decision-Makers

Learning From the Companies Driving Clinical Progress

Mechanistic Insights into Splicing Modulation to Define RNA-Small Molecule Interactions & Unlock Targetable Splice Sequences

Conference Day One

Speaker:

  • Christopher Trotta, Senior Vice President of Discovery Biology, PTC Therapeutics

Gain insight into how one of the most established organizations in the field is expanding targetable RNA sequences and progressing therapeutically relevant programs.

PTC Therapeutics
Understanding How the Landscape Is Evolving Beyond Splice Modulation

RNA Methyltransferase Inhibition Validates Epitranscriptomic Regulation as a Novel Approach in the Treatment of Solid Tumors

Conference Day Two

Speaker:

  • Andrea Casazza, Head of Cancer Biology, EPICS Therapeutics

Explore how novel mechanisms and therapeutic approaches are expanding the commercial opportunity within RNA-targeted drug discovery.

epics therapeutics logo
Preparing for the Future of RNA-Targeted Drug Discovery

Panel Discussion: Establishing RNA-Targeted Small Molecules as a Generalizable Drug Modality

Conference Day Two

Speakers:

  • Yann Foricher, Head of Small Molecules Medicinal Chemistry, Sanofi
  • Tom Chappie, Senior Principal Scientist & Research Fellow, Pfizer
  • Nikolai Naryshkin, Chief Scientific Officer, Ribonaut Therapeutics

Hear industry leaders debate the evidence, technologies, disease areas, and translational milestones required to establish RNA targeting as the next major drug discovery modality.

Tom Chappie
Sanofi logo
Pfizer logo
Ribonaut Therapeutics

Benchmark Your Strategy Against Peers

Questions you could ask your peers to benchmark against them:

How are leading companies differentiating their RNA-targeting platforms?

What milestones are pharma partners looking for?

Which modalities are attracting the greatest investment?

How are companies balancing platform development versus asset progression?

What will define success in RNA-targeted therapeutics over the next 3–5 years?

What Past Attendees Say

PTC Therapeutics

The RNA conference provides the best opportunity to engage with the largest number of RNA-targeting companies, most of whom attend other conferences but rarely the same ones.

Veritas In Silico

I greatly enjoyed the panel discussions, which were highly interactive and offered different perspectives from leaders in the field. It was particularly exciting to learn about the new chemical entities currently in clinical trials, as well as the novel strategies for RNA modulation and tools for discovery. Overall, the summit was both informative and inspiring, giving me valuable insights and ideas that I can bring back to my own work.

Turn RNA Innovation Into Action

From identifying functional RNA targets and optimizing lead compounds to securing strategic partnerships and evaluating new modalities, this summit is designed to help you overcome the challenges facing the next generation of RNA-targeted therapeutics.

Explore the latest scientific advances, connect with peers facing similar challenges, and leave with practical insights you can immediately apply to your research, pipeline, and business strategy.

Secure your place today or explore the full agenda to discover the sessions most relevant to you.