Targeting HTT RNA & Translation for Allele-Selective Lowering of Mutant Huntington
Time: 1:45 pm
day: Conference Day Two
Details:
• Validating HTT exon1 as a target for allele-selective targeting in HD
• Identifying and profiling of allele-preferential HTT RNA binding small molecules
• Exploring opportunities for targeting uORF regulatory mechanisms in HTT translation
