Utilizing RNA-Seq Data At-Scale to Improve the Translatability of mRNA Splicing Modulators

Time: 11:30 am
day: Focus Day

Details:

  • Outlining the unique translational challenges in developing small molecule modulators of mRNA splicing
  • Summarizing use of multi-dose RNA-seq experiments to identify potentially toxic off target liabilities for development candidates
  • Summarizing use of multi-species RNA-seq data to improve animal model selection during preclinical research

Speakers: