Genetic Medicines: Discovering Small Molecules that Interdict RNA Function
Time: 2:00 pm
day: Day One
Details:
- RNA targets are now broadly validated clinically and commercially, but many attractive targets remain out of reach to current modalities
- Arrakis has built a novel and highly differentiated platform for discovering drug-like small molecule ligands for RNA targets
- Arrakis platform has thus far produced at least two small molecule programs that clearly mimic the biological activity of oligonucleotide therapeutics
