PTC Therapeutics
PTC is a global biopharmaceutical company that discovers, develops, and commercializes clinically differentiated medicines for children and adults living with serious diseases of high unmet need. The alternative RNA splicing technology has broad potential to identify new treatments for many diseases. We believe that we can identify other small molecules that modify alternative splicing of genes, promote inclusion of specific exons, or force skipping of undesired exons from the mature mRNA. We continue to build on our alternative RNA splicing platform to develop innovative therapies that address the underlying causes of life-limiting diseases.
