Emily Garcia Sega
Seminars
Wednesday 11th November 2026
Restoring Splicing Function in DM1 by Selectively Targeting Toxic CUGRepeat RNA
4:30 pm
- Selectively targeting toxic CUG-repeat RNA in DM1
- Disrupting RNA foci to release MBNL1
- Linking target engagement to restored splicing function
- Building confidence in potency, selectivity and disease relevance
