Optimizing Chemical Matter Against RNA to Improve Therapeutics: Lessons from Rgenta’s RNA-Targeted Platform

Time: 4:15 pm
day: Conference Day One

Details:

• Introducing Rgenta’s RNA-targeting small molecule platform and its approach to addressing disease-relevant RNA targets

• Highlighting case studies from lead programs in ACC & Huntington’s disease to showcase platform-driven success in drug discovery

• Sharing insights on generating and refining small molecules as RNA splice modulators, including strategies for modeling splice sites

Speakers: