Targeting mRNA Biology in a Tissue Selective & Disease-Specific Manner with Small Molecules

Time: 12:15 pm
day: Day Two


• mRNA Lightning: a novel platform for the discovery of selective small molecule mRNA drugs and their mechanisms of action
• Selectivity of mRNA biology: tissue selectivity in mRNA translation regulation, in mRNA transport and localization
• Wholly owned pipeline of 18 programs including among others: fibrosis (collagen I translation inhibitors for fibrotic diseases), oncology (c-MYC and K-RAS translation), and neuroscience (Tau translation inhibitors)